14th International Congress on Antiphospholipid Antibodies Task Force Report on Antiphospholipid Syndrome Treatment Trends

Carregando...
Imagem de Miniatura
Citações na Scopus
268
Tipo de produção
article
Data de publicação
2014
Título da Revista
ISSN da Revista
Título do Volume
Editora
ELSEVIER SCIENCE BV
Autores
ERKAN, Doruk
AGUIAR, Cassyanne L.
COHEN, Hannah
CUADRADO, Maria J.
DANOWSKI, Adriana
LEVY, Roger A.
ORTEL, Thomas L.
RAHMAN, Anisur
SALMON, Jane E.
Citação
AUTOIMMUNITY REVIEWS, v.13, n.6, p.685-696, 2014
Projetos de Pesquisa
Unidades Organizacionais
Fascículo
Resumo
Antiphospholipid Syndrome (APS) is characterized by vascular thrombosis and/or pregnancy morbidity occurring in patients with persistent antiphospholipid antibodies (aPL). The primary objective of the APS Treatment Trends Task Force, created as part of the 14th International Congress on aPL, was to systematically review the potential future treatment strategies for aPL-positive patients. The task force chose as future clinical research directions: a) determining the necessity for controlled clinical trials in venous thromboembolism with the new oral direct thrombin or anti-factor Xa inhibitors pending the results of the ongoing rivaroxaban in APS (RAPS) trial, and designing controlled clinical trials in other forms of thrombotic APS; b) systematically analyzing the literature as well as aPL/APS registries, and creating specific registries for non-warfarin/heparin anticoagulants; c) increasing recruitment for an ongoing primary thrombosis prevention trial, and designing secondary thrombosis and pregnancy morbidity prevention trials with hydroxychloroquine; d) determining surrogate markers to select patients for statin trials; e) designing controlled studies with rituximab and other and-B-cell agents; f) designing mechanistic and clinical studies with eculizumab and other complement inhibitors; and g) chemically modifying peptide therapy to improve the half-life and minimize immunogenicity. The report also includes recommendations for clinicians who consider using these agents in difficult-to-manage aPL-positive patients.
Palavras-chave
Antiphospholipid syndrome, Oral direct thrombin inhibitors, Hydroxychloroquine, Statins, Complement and B-cell inhibition, Peptide therapy
Referências
  1. Ageno W, 2013, J Thromb Haemost, V11, P177, DOI 10.1111/jth.12038
  2. Agmon-Levin N, 2011, ANN RHEUM DIS, V70, P145, DOI 10.1136/ard.2010.134817
  3. Agmon-Levin N, 2013, CLIN REV ALLERG IMMU, V45, P256, DOI 10.1007/s12016-012-8342-y
  4. Agnelli G, 2013, NEW ENGL J MED, V369, P799, DOI 10.1056/NEJMoa1302507
  5. Aguiar CL, 2013, APLA LACA
  6. Akkerman A, 2004, AUTOIMMUNITY, V37, P445, DOI 10.1080/0891693040008524
  7. Ames PRJ, 2010, LUPUS, V19, P711, DOI 10.1177/0961203309357765
  8. Ames PRJ, 2007, ANN HEMATOL, V86, P227, DOI 10.1007/s00277-006-0226-x
  9. Andreoli L, 2012, LUPUS, V21, P736, DOI 10.1177/0961203312446386
  10. [Anonymous], 2011, LIX ED 15 MG 30 MG T
  11. [Anonymous], SUMM PROD CHAR SPC E
  12. Baglin T, 2012, BRIT J HAEMATOL, V159, P427, DOI 10.1111/bjh.12052
  13. EINSTEIN Investigators, 2010, N Engl J Med, V363, P2499, DOI 10.1056/NEJMoa1007903
  14. Berman H, 2013, AUTOIMMUN REV, V12, P1085, DOI 10.1016/j.autrev.2013.05.004
  15. Blank M, 1999, P NATL ACAD SCI USA, V96, P5164, DOI 10.1073/pnas.96.9.5164
  16. Bouma B, 1999, EMBO J, V18, P5166, DOI 10.1093/emboj/18.19.5166
  17. Broder A, 2013, J RHEUMATOL, V40, P30, DOI 10.3899/jrheum.120157
  18. Broder A, 2009, ARTHRITIS RHEUM S10, V60, P279
  19. Bulla R, 2005, CHEM IMMUNOL ALLERGY, V89, P149
  20. Buller HR, 2012, NEW ENGL J MED, V366, P1287
  21. Castellone DD, 2010, AM J HEMATOL, V85, P185, DOI 10.1002/ajh.21607
  22. Costa Rubens, 2013, Clin Rheumatol, V32 Suppl 1, pS79, DOI 10.1007/s10067-010-1506-3
  23. Costedoat-Chalumeau N, 2007, ANN RHEUM DIS, V66, P821, DOI 10.1136/ard.2006.067835
  24. Costedoat-Chalumeau N, 2007, RHEUMATOLOGY, V46, P808, DOI 10.1093/rheumatology/ke1402
  25. Cuadrado MJ, 1997, ARTHRITIS RHEUM, V40, P834, DOI 10.1002/art.1780400509
  26. Danesh FR, 2003, ARCH IMMUNOL THER EX, V51, P139
  27. de la Torre YM, 2012, J AUTOIMMUN, V38, pJ209, DOI 10.1016/j.jaut.2011.11.009
  28. de Leeuw K, 2006, LUPUS, V15, P675, DOI 10.1177/0961203306069972
  29. DeZern AE, 2013, EUR J HAEMATOL, V90, P16, DOI 10.1111/ejh.12021
  30. Edwards MH, 1997, CIRCULATION, V96, P4380
  31. Eerenberg ES, 2011, CIRCULATION, V124, P1573, DOI 10.1161/CIRCULATIONAHA.111.029017
  32. Eikelboom JW, 2013, NEW ENGL J MED, V369, P1206, DOI 10.1056/NEJMoa1300615
  33. Elalamy I, 2008, J THROMB HAEMOST, V6, P1242, DOI 10.1111/j.1538-7836.2008.02973.x
  34. Erdozain J G, 2004, Haematologica, V89, pECR34
  35. Erkan D, 2013, ANN RHEUM DIS
  36. Erkan D, 2002, RHEUMATOLOGY, V41, P924, DOI 10.1093/rheumatology/41.8.924
  37. Erkan D, 2005, ANN RHEUM DIS, V64, P1321, DOI 10.1136/ard.2004.031856
  38. Erkan D, 2013, ARTHRITIS RHEUM-US, V65, P464, DOI 10.1002/art.37759
  39. Erre GL, 2008, LUPUS, V17, P50, DOI 10.1177/0961203307085251
  40. Ferrara DE, 2004, J THROMB HAEMOST, V2, P1558, DOI 10.1111/j.1538-7836.2004.00896.x
  41. Ferrara DE, 2003, ARTHRITIS RHEUM, V48, P3272, DOI 10.1002/art.11449
  42. Fleisher LA, 2008, ANESTH ANALG, V106, P685, DOI 10.1213/01/ane.0000309024.28586.70
  43. Frances C, 2012, ARCH DERMATOL, V148, P479, DOI 10.1001/archdermatol.2011.2558
  44. Gharavi AE, 2003, LUPUS, V12, P579, DOI 10.1191/0961203303lu448rr
  45. Gharavi AE, 2002, ARTHRITIS RHEUM, V46, P545, DOI 10.1002/art.10130
  46. Giannakopoulos B, 2007, BLOOD, V109, P422, DOI 10.1182/blood-2006-04-001206
  47. Girardi G, 2003, J CLIN INVEST, V112, P1644, DOI 10.1172/JCI18817
  48. Girardi G, 2004, NAT MED, V10, P1222, DOI 10.1038/1121
  49. Glynn RJ, 2009, NEW ENGL J MED, V360, P1851, DOI 10.1056/NEJMoa0900241
  50. Hillmen P, 2004, NEW ENGL J MED, V350, P552, DOI 10.1056/NEJMoa031688
  51. Hillmen P, 2006, NEW ENGL J MED, V355, P1233, DOI 10.1056/NEJMoa061648
  52. Hindler K, 2006, ANESTHESIOLOGY, V105, P1260, DOI 10.1097/00000542-200612000-00027
  53. Ho KT, 2005, RHEUMATOLOGY, V44, P1303, DOI 10.1093/rheumatology/kei014
  54. Holtan SG, 2006, J THROMB HAEMOST, V4, P1632, DOI 10.1111/j.1538-7836.2006.01961.x
  55. Huang HC, 2010, P NATL ACAD SCI USA, V107, P4658, DOI 10.1073/pnas.1001074107
  56. HUNT J, 1994, J IMMUNOL, V152, P653
  57. Ioannou Y, 2007, ARTHRITIS RHEUM-US, V56, P280, DOI 10.1002/ary.22306
  58. Ioannou Y, 2009, J THROMB HAEMOST, V7, P833, DOI 10.1111/j.1538-7836.2009.03316.x
  59. Iverson GM, 2002, J IMMUNOL, V169, P7097
  60. Iverson GM, 1998, P NATL ACAD SCI USA, V95, P15542, DOI 10.1073/pnas.95.26.15542
  61. JOHNSON R, 1979, CLIN ORTHOP RELAT R, P174
  62. Jung HJ, 2010, ARTHRITIS RHEUM-US, V62, P863, DOI 10.1002/art.27289
  63. Kahn P, 2008, ARTHRITIS RHEUM, V58, P2824, DOI 10.1002/art.23764
  64. Kaiser R, 2009, ANN RHEUM DIS, V68, P238, DOI 10.1136/ard.2008.093013
  65. Khattri S, 2012, AUTOIMMUN REV, V11, P717, DOI 10.1016/j.autrev.2011.12.011
  66. Khianey R, 2013, APLA LACA
  67. Klack K, 2010, JOINT BONE SPINE, V77, P489, DOI 10.1016/j.jbspin.2010.02.043
  68. Kumar Deepak, 2010, Curr Rheumatol Rep, V12, P40, DOI 10.1007/s11926-009-0074-5
  69. Lauvao LS, 2008, J VASC SURG, V48, P472, DOI 10.1016/j.jvs.2008.02.052
  70. Legendre CM, 2013, NEW ENGL J MED, V368, P2169, DOI 10.1056/NEJMoa1208981
  71. Levine AB, 2012, ACR
  72. Linkins LA, 2012, CHEST S, V141, pe495S
  73. Lockshin MD, 2010, J REPROD IMMUNOL, V84, P206, DOI 10.1016/j.jri.2009.11.007
  74. Lonze BE, 2010, NEW ENGL J MED, V362, P1744, DOI 10.1056/NEJMc0910965
  75. Lopez-Pedrera C, 2011, ANN RHEUM DIS, V70, P675, DOI 10.1136/ard.2010.135525
  76. Majka DS, 2013, INFLAMM RES, V62, P919, DOI 10.1007/s00011-013-0652-x
  77. Marmor MF, 2011, OPHTHALMOLOGY, V118, P415, DOI 10.1016/j.ophtha.2010.11.017
  78. Martinez-Martinez LA, 2007, CLIN EXP RHEUMATOL, V25, P18
  79. Martinuzzo ME, 2013, INT J LAB HEMATOL
  80. Medina G, 2011, AUTOIMMUN REV, V10, P214, DOI 10.1016/j.autrev.2010.10.004
  81. Meroni PL, 2001, ARTHRITIS RHEUM, V44, P2870, DOI 10.1002/1529-0131(200112)44:12<2870::AID-ART475>3.0.CO;2-Y
  82. Merriman E, 2011, THROMB HAEMOSTASIS, V105, P385, DOI 10.1160/TH10-08-0511
  83. Miyakis S, 2006, J THROMB HAEMOST, V4, P295, DOI 10.1111/j.1538-7836.2006.01753.x
  84. Mok CC, 2005, ARTHRITIS RHEUM, V52, P2774, DOI 10.1002/art.21224
  85. Mok MY, 2005, J RHEUMATOL, V32, P622
  86. Nurnberger J, 2009, NEW ENGL J MED, V360, P542, DOI 10.1056/NEJMc0808527
  87. Odiari EA, 2012, HUM REPROD, V27, P2933, DOI 10.1093/humrep/des288
  88. Ostertag MV, 2006, LUPUS, V15, P358, DOI 10.1191/0961203306lu2315oa
  89. Ota K, 2013, HUM REPROD
  90. Paupitz JA, 2010, LUPUS, V19, P1302, DOI 10.1177/0961203310372938
  91. Peerschke EI, 2010, MOL IMMUNOL, V47, P2170, DOI 10.1016/j.molimm.2010.05.009
  92. Pericleous C, 2011, MOL IMMUNOL, V49, P56, DOI 10.1016/j.molimm.2011.07.024
  93. Pericleous C, 2010, ARTHRITIS RHEUM, V62, pS563
  94. Petri M., 1994, Arthritis and Rheumatism, V37, pS297
  95. Petri M, 2013, APLA LACA
  96. Piantoni S, 2012, Reumatismo, V64, P307, DOI 10.4081/reumatismo.2012.307
  97. Pickering MC, 2007, J EXP MED, V204, P1249, DOI 10.1084/jem.20070301
  98. Pierangeli SS, 1999, CIRCULATION, V99, P1997
  99. Pierangeli SS, 2004, J AUTOIMMUN, V22, P217, DOI 10.1016/j/jaut.2004.01.002
  100. Rand JH, 2010, BLOOD, V115, P2292, DOI 10.1182/blood-2009-04-213520
  101. Rand JH, 2008, BLOOD, V112, P1687, DOI 10.1182/blood-2008-03-144204
  102. Redecha P, 2007, BLOOD, V110, P2423, DOI 10.1182/blood-2007-01-070631
  103. Redecha P, 2008, J CLIN INVEST, V118, P3453, DOI 10.1172/JCI36089
  104. Ridker PM, 2009, LANCET, V373, P1175, DOI 10.1016/S0140-6736(09)60447-5
  105. Ritis K, 2006, J IMMUNOL, V177, P4794
  106. Rota E, 2008, THROMB HAEMOSTASIS, V99, P779, DOI 10.1160/TH07-09-0573
  107. Rubenstein E, 2006, J RHEUMATOL, V33, P355
  108. Ruiz-Irastorza G, 2010, ANN RHEUM DIS, V69, P20, DOI 10.1136/ard.2008.101766
  109. Ruiz-Irastorza G, 2006, LUPUS, V15, P577, DOI 10.1177/0961203306071872
  110. Sacre K, 2012, ARTHRITIS RES THER, V14, DOI 10.1186/ar3895
  111. Salem M, 2010, THROMB HAEMOSTASIS, V104, P1071, DOI [10.1160/TH10-05-0284, 10.1160/TH10.05.0284]
  112. Salmon JE, 2011, PLOS MED, V8, DOI 10.1371/journal.pmed.1001013
  113. Samama MM, 2011, CLIN CHEM LAB MED, V49, P761, DOI 10.1515/CCLM.2011.134
  114. Samama MM, 2010, THROMB HAEMOSTASIS, V103, P815, DOI 10.1160/TH09-03-0176
  115. Schmidt-Tanguy A, 2013, J THROMB HAEMOST, V11, P1927, DOI 10.1111/jth.12363
  116. Schulman S, 2009, N ENGL MED, V361, P2341
  117. Sciascia S, 2011, LUPUS, V20, P1106, DOI 10.1177/0961203311400115
  118. Shapira I, 2012, ARTHRITIS RHEUM-US, V64, P2719, DOI 10.1002/art.34440
  119. Simantov E, 1995, J CLIN INVEST, V96, P2211
  120. Sinibaldi S, 2013, PEDIATR TRANSPLANT, V17, pE177, DOI 10.1111/petr.12151
  121. Stohl W, 2012, ARTHRITIS RHEUM-US, V64, P2328, DOI 10.1002/art.34400
  122. Summary of product characteristics (SPC), SUMM PROD CHAR SPC E
  123. Summary of product characteristics (SPC), 2011, SUMM PROD CHAR SPC E
  124. Summary of product characteristics (SPC), SUMM PROD CHAR SPC E
  125. Tektonidou MG, 2009, ARTHRIT RHEUM-ARTHR, V61, P29, DOI 10.1002/art.24232
  126. Tenedios F, 2005, ARTHRITIS RHEUM, V52, P4078
  127. Buller HR, 2013, NEW ENGL J MED, V369, P1406, DOI 10.1056/NEJMoa1306638
  128. Tommasino C, 2004, THROMB RES, V114, P652
  129. Trappe R, 2006, ANN HEMATOL, V85, P134, DOI 10.1007/s00277-005-0028-6
  130. Tripodi A, 2001, BRIT J HAEMATOL, V115, P672, DOI 10.1046/j.1365-2141.2001.03178.x
  131. Tsagalis G, 2011, ARTIF ORGANS, V35, P420, DOI 10.1111/j.1525-1594.2010.01068.x
  132. Urowitz MB, 2010, ARTHRIT CARE RES, V62, P881, DOI 10.1002/acr.20122
  133. Van Os GMA, 2011, J THROMB HAEMOST, V9, P1657, DOI 10.1111/j.1538-7836.2011.04395.x
  134. WALLACE DJ, 1987, ARTHRITIS RHEUM, V30, P1435, DOI 10.1002/art.1780301219
  135. Warkentin TE, 2008, J THROMB HAEMOST, V6, P1243, DOI 10.1111/j.1538-7836.2008.2972.x
  136. Warkentin TE, 2007, NEW ENGL J MED, V356, P2653
  137. Watson H, 2012, BRIT J HAEMATOL, V159, P528, DOI 10.1111/bjh.12059
  138. Wu XX, 2011, AM J OBSTET GYNECOL, V205, pe7
  139. Xu CG, 2000, SCIENCE, V287, P498, DOI 10.1126/science.287.5452.498
  140. Youinou P, 2004, THROMB RES, V114, P363, DOI 10.1016/j.thromres.2004.06.019